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  • Wednesday, Jun 11th
    8:30 AM - 10:00 AM HK Time
    CLINICAL TRIAL UPDATES
    Location: Theater 1, L1
    Co-Chair: Tenneille Ludwig, PhD (she/her/hers) – WiCell Research Institute
    Co-Chair: Arnold R. Kriegstein, MD, PhD – University of California, San Francisco
    Presenting Author: Clive N. Svendsen, PhD – Cedars-Sinai Board of Governors Regenerative Medicine Institute
    Presenting Author: Michael Davis, PhD – Emory University
    Presenting Author: Andres Bratt-Leal, PhD – Aspen Neuroscience Inc.
    Presenting Author: Jun Takahashi, MD, PhD – Center for iPS Cell Research and Application (CiRA), Kyoto University
    Clinical Applications
  • Wednesday, Jun 11th
    8:35 AM - 8:55 AM HK Time
    A CLINICAL TRIAL TRANSPLANTING HUMAN NEURAL PROGENITORS SECRETING GDNF INTO THE MOTOR CORTEX OF ALS PATIENTS: SURVIVAL AND MIGRATION INTO REGIONS OF DYING MOTOR NEURONS TO ENGAGE TARGET
    Location: Theater 1, L1
    Presenting Author: Clive N. Svendsen, PhD – Cedars-Sinai Board of Governors Regenerative Medicine Institute
    Clinical Applications
  • Wednesday, Jun 11th
    8:55 AM - 9:15 AM HK Time
    PHASE 1 RANDOMIZED STUDY OF CARDIAC STEM CELLS IN PATIENTS WITH HYPOPLASTIC LEFT HEART SYNDROME: CHILD TRIAL
    Location: Theater 1, L1
    Presenting Author: Michael Davis, PhD – Emory University
    Clinical Applications
  • Wednesday, Jun 11th
    9:15 AM - 9:35 AM HK Time
    SAFETY, TOLERABILITY, AND EFFICACY OF TRANSPLANTED AUTOLOGOUS IPSC-DERIVED DOPAMINERGIC PRECURSORS IN MODERATE TO ADVANCED PARKINSON’S DISEASE
    Location: Theater 1, L1
    Presenting Author: Andres Bratt-Leal, PhD – Aspen Neuroscience Inc.
    Clinical Applications
  • Wednesday, Jun 11th
    9:35 AM - 9:55 AM HK Time
    IPSC-BASED THERAPY FOR PARKINSON’S DISEASE
    Location: Theater 1, L1
    Presenting Author: Jun Takahashi, MD, PhD – Center for iPS Cell Research and Application (CiRA), Kyoto University
    Clinical Applications
  • Thursday, Jun 12th
    8:30 AM - 10:00 AM HK Time
    REVOLUTIONIZING THERAPIES FOR CHRONIC DISEASES
    Location: Theater 2, L1
    Co-Chair: Evan L. Lee Graham, PhD (he/him/his) – BioLamina
    Co-Chair: Ken Zaret, PhD (he/him/his) – Perelman School of Medicine, University of Pennsylvania
    Concurrent Speaker: Jihwan Song, D Phil – Department of Biomedical Sciences, CHA University I iPS Bio, Inc.
    Presenting Author: Rosario Isasi, JD MPH (she/her/hers) – University of Miami
    Presenting Author: Sarah Kieler Saietz, MSc, BSc (she/her/hers) – Karolinska Institutet
    Presenting Author: Mo Li, PhD – King Abdullah University of Science and Technology (KAUST)
    Presenting Author: Alice Del Vecchio – Istituto di Ricerche Farmacologiche Mario Negri IRCCS
    Concurrent Speaker: Hongkui Deng, PhD – Peking University
    Clinical Applications
  • Thursday, Jun 12th
    8:35 AM - 8:55 AM HK Time
    Developing iPSC-Based Cell Therapy for Huntington's Disease
    Location: Theater 2, L1
    Concurrent Speaker: Jihwan Song, D Phil – Department of Biomedical Sciences, CHA University I iPS Bio, Inc.
    Clinical Applications
  • Thursday, Jun 12th
    8:55 AM - 9:05 AM HK Time
    “THE REGULATORY SYSTEM IS CAPABLE OF HANDLING MOST OF THE SCARY SCENARIOS THAT PEOPLE THROW UP”: KEY INFORMANT PERSPECTIVES ON PRENATAL GENE EDITING
    Location: Theater 2, L1
    Presenting Author: Rosario Isasi, JD MPH (she/her/hers) – University of Miami
    Clinical Applications
  • Thursday, Jun 12th
    9:05 AM - 9:15 AM HK Time
    DEVELOPMENT AND PRECLINICAL VALIDATION OF CELLTHRPE1: A STEM CELL-DERIVED RETINAL THERAPY FOR DRY AGE-RELATED MACULAR DEGENERATION
    Location: Theater 2, L1
    Presenting Author: Sarah Kieler Saietz, MSc, BSc (she/her/hers) – Karolinska Institutet
    Clinical Applications
  • Thursday, Jun 12th
    9:15 AM - 9:25 AM HK Time
    CRISPR-CAS9-INDUCED DOUBLE-STRAND BREAKS DISRUPT MAINTENANCE OF EPIGENETIC INFORMATION
    Location: Theater 2, L1
    Presenting Author: Mo Li, PhD – King Abdullah University of Science and Technology (KAUST)
    Clinical Applications
  • Thursday, Jun 12th
    9:25 AM - 9:35 AM HK Time
    ENGINEERED HUMAN TUBULES REVEAL PATHOPHYSIOLOGICAL MECHANISMS OF AUTOSOMAL DOMINANT POLYCYSTIC KIDNEY DISEASE
    Location: Theater 2, L1
    Presenting Author: Alice Del Vecchio – Istituto di Ricerche Farmacologiche Mario Negri IRCCS
    Clinical Applications
  • Thursday, Jun 12th
    9:35 AM - 9:55 PM HK Time
    HONGKUI DENG TITLE COMING SOON
    Location: Theater 2, L1
    Concurrent Speaker: Hongkui Deng, PhD – Peking University
    Clinical Applications
  • Thursday, Jun 12th
    2:00 PM - 3:30 PM HK Time
    MODULATING THE IMMUNE SYSTEM TO FIGHT DISEASE
    Location: Theater 1, L1
    Co-Chair: Gordon Keller, PhD – McEwen Stem Cell Institute, University Health Network
    Co-Chair: Jaime Imitola, MD (he/him/his) – Deparment of Neurology University of Connecticut
    Concurrent Speaker: Megan Levings, PhD – University of British Columbia
    Presenting Author: Asuka Morizane, PhD MD – Kobe City Medical Center General Hospital
    Presenting Author: Marco Cortese, PhD (he/him/his) – Candiolo Cancer Institute
    Presenting Author: Yasunori Aizawa, PhD – Logomix, Inc.
    Presenting Author: Lili Yang, PhD – University of California, Los Angeles (UCLA)
    Concurrent Speaker: John Rasko – Cynata Therapeutics
    Clinical Applications
  • Thursday, Jun 12th
    2:05 PM - 2:25 PM HK Time
    BUILDING AN ENHANCED IMMUNE SYSTEM TO FIGHT DISEASE
    Location: Theater 1, L1
    Concurrent Speaker: Megan Levings, PhD – University of British Columbia
    Clinical Applications
  • Thursday, Jun 12th
    2:25 PM - 2:35 PM HK Time
    IMMUNE RESPONSE IN IPSC-BASED ALLOGENEIC CELL THERAPY FOR PARKINSON'S DISEASE
    Location: Theater 1, L1
    Presenting Author: Asuka Morizane, PhD MD – Kobe City Medical Center General Hospital
    Clinical Applications
  • Thursday, Jun 12th
    2:35 PM - 2:45 PM HK Time
    SYNNOTCH/CAR-BASED COMBINATORIAL IMMUNOTHERAPY AGAINST COLORECTAL CANCER WITH HER2 AMPLIFICATION IN NK AND IPSC-DERIVED NK CELLS.
    Location: Theater 1, L1
    Presenting Author: Marco Cortese, PhD (he/him/his) – Candiolo Cancer Institute
    Clinical Applications
  • Thursday, Jun 12th
    2:55 PM - 3:05 PM HK Time
    GENERATION OF ALLOGENEIC CAR-NKT CELLS FROM HEMATOPOIETIC STEM AND PROGENITOR CELLS USING A CLINICALLY GUIDED CULTURE METHOD
    Location: Theater 1, L1
    Presenting Author: Lili Yang, PhD – University of California, Los Angeles (UCLA)
    Clinical Applications
  • Thursday, Jun 12th
    3:05 PM - 3:25 PM HK Time
    FIRST HUMAN CLINICAL TRIALS OF iPSC-DERIVED MSCs
    Location: Theater 1, L1
    Concurrent Speaker: John Rasko – Cynata Therapeutics
    Clinical Applications
  • Friday, Jun 13th
    8:30 AM - 10:00 AM HK Time
    CLINICAL TRANSLATION OF BIOENGINEERED TISSUE-BASED THERAPEUTICS
    Location: Hall 3F, L3
    Co-Chair: Denise Zujur, PhD – Center for iPS Cell Research and Application (CiRA), Kyoto University
    Co-Chair: William J. Anderson – Harvard University
    Concurrent Speaker: Ryuichi Okamoto, MD, PhD (he/him/his) – Institute of Science Tokyo
    Presenting Author: Kevin D. Costa – Novoheart, Medera Biopharm
    Presenting Author: Wei Zuo, PhD (he/him/his) – Tongji University
    Presenting Author: Shin-Jeong Lee, PhD – Yonsei University
    Presenting Author: Marcelo N. Rivolta, MD PhD – University of Sheffield and Rinri Therapeutics
    Concurrent Speaker: Xin Cheng, PhD – Shanghai Institute of Biochemistry and Cell Biology
    Clinical Applications
    Sponsored By 
  • Friday, Jun 13th
    8:35 AM - 8:55 AM HK Time
    CLINICAL APPLICATION OF PATIENT-DERIVED ORGANOIDS IN THE TREATMENT OF INFLAMMATORY BOWEL DISEASE
    Location: Hall 3F, L3
    Concurrent Speaker: Ryuichi Okamoto, MD, PhD (he/him/his) – Institute of Science Tokyo
    Clinical Applications
  • Friday, Jun 13th
    8:55 AM - 9:05 AM HK Time
    GENE THERAPY CLINICAL TRIAL FOR HEART FAILURE WITH PRESERVED EJECTION FRACTION (MUSIC-HFPEF) INFORMED BY IN VITRO SCREENING WITH STEM CELL-BASED BIOENGINEERED MINI-HEARTS
    Location: Hall 3F, L3
    Presenting Author: Kevin D. Costa – Novoheart, Medera Biopharm
    Clinical Applications
  • Friday, Jun 13th
    9:05 AM - 9:15 AM HK Time
    AUTOLOGOUS TRANSPLANTATION OF AIRWAY BASAL STEM CELLS IN COPD PATIENTS: A RANDOMIZED, SINGLE-BLIND, PLACEBO-CONTROLLED PHASE 2 TRIAL
    Location: Hall 3F, L3
    Presenting Author: Wei Zuo, PhD (he/him/his) – Tongji University
    Clinical Applications
  • Friday, Jun 13th
    9:15 AM - 9:25 AM HK Time
    PRECLINICAL STUDY OF HUMAN INDUCED PLURIPOTENT STEM CELL-DERIVED ENDOTHELIAL CELLS FOR PERIPHERAL ARTERY DISEASE
    Location: Hall 3F, L3
    Presenting Author: Shin-Jeong Lee, PhD – Yonsei University
    Clinical Applications
  • Friday, Jun 13th
    9:25 AM - 9:35 AM HK Time
    DEVELOPING A PSC-DERIVED THERAPY FOR HEARING LOSS: PAVING THE WAY FOR A FIRST-IN-HUMAN CLINICAL TRIAL
    Location: Hall 3F, L3
    Presenting Author: Marcelo N. Rivolta, MD PhD – University of Sheffield and Rinri Therapeutics
    Clinical Applications
  • Friday, Jun 13th
    9:35 AM - 9:55 AM HK Time
    ENDODERM STEM-CELL DERIVED ISLET TISSUE FOR THERAPEUTICS & DISEASE MODELING
    Location: Hall 3F, L3
    Concurrent Speaker: Xin Cheng, PhD – Shanghai Institute of Biochemistry and Cell Biology
    Clinical Applications
  • Friday, Jun 13th
    2:00 PM - 3:30 PM HK Time
    EXPANDING THERAPEUTICS THROUGH STEM CELLS AND REPROGRAMMING
    Location: Convention Hall C, L1
    Co-Chair: Athanasia D. Panopoulos, PhD – Cedars-Sinai Medical Center
    Co-Chair: Xian Weng (he/him/his) – Mytos
    Concurrent Speaker: Maria Pia Cosma, PhD – Centre for Genomic Regulation
    Presenting Author: Jean Paul Chadarevian, PhD – University of California, Irvine
    Presenting Author: Rongrong Wu, PhD (she/her/hers) – Zhejiang University
    Presenting Author: Dong-Wook Kim, PhD – Yonsei Univ College of Medicine
    Presenting Author: Keisuke Kaji, PhD – University of Edinburgh
    Concurrent Speaker: Pentao Liu, PhD (he/him/his) – The University of Hong Kong
    Clinical Applications
    Sponsored By 
  • Friday, Jun 13th
    2:05 PM - 2:25 PM HK Time
    STRATEGIES AND ADVANCES IN REGENERATING AND SUSTAINING NEURAL TISSUE
    Location: Convention Hall C, L1
    Concurrent Speaker: Maria Pia Cosma, PhD – Centre for Genomic Regulation
    Clinical Applications
  • Friday, Jun 13th
    2:25 PM - 2:35 PM HK Time
    ENGINEERING IPSC-DERIVED MICROGLIA FOR IMMUNE CELL-BASED THERAPIES FOR NEUROLOGICAL DISEASES
    Location: Convention Hall C, L1
    Presenting Author: Jean Paul Chadarevian, PhD – University of California, Irvine
    Clinical Applications
  • Friday, Jun 13th
    2:35 PM - 2:45 PM HK Time
    LYOPHILIZED EXTRACELLULAR VESICLES PROMOTE CARDIOMOCYTE SURVIVAL AND PROLIFERATION VIA STC2- MEDIATED GLUCOSE METABOLISM IN ISCHEMIC HEART INJURY
    Location: Convention Hall C, L1
    Presenting Author: Rongrong Wu, PhD (she/her/hers) – Zhejiang University
    Clinical Applications
  • Friday, Jun 13th
    2:45 PM - 2:55 PM HK Time
    PHASE 1/2A CLINICAL TRIAL OF HUMAN ESC-DERIVED DOPAMINE NEURONS FOR PARKINSON’S DISEASE
    Location: Convention Hall C, L1
    Presenting Author: Dong-Wook Kim, PhD – Yonsei Univ College of Medicine
    Clinical Applications
  • Friday, Jun 13th
    2:55 PM - 3:05 PM HK Time
    PRECURSOR OF CHEMICALLY EXPANDED HEPATOCYTES (PRE-CHEP) WITH 1 MILLION-FOLD EXPANSION POTENTIAL AND LIVER REPOPULATION CAPACITIY
    Location: Convention Hall C, L1
    Presenting Author: Keisuke Kaji, PhD – University of Edinburgh
    Clinical Applications
  • Friday, Jun 13th
    3:05 PM - 3:25 PM HK Time
    HUMAN EXPANDED POTENTIAL STEM CELLS FOR FUNDAMENTAL RESEARCH AND TRANSLATIONAL APPLICATIONS
    Location: Convention Hall C, L1
    Concurrent Speaker: Pentao Liu, PhD (he/him/his) – The University of Hong Kong
    Clinical Applications