Claire Booth, MBBS MSc PhD FRCPCH (she/her/hers)

UCL Great Ormond Street Institute of Child Health, United Kingdom

Claire is a Professor of Paediatric Immunology and Gene Therapy at UCL Great Ormond Street Institute of Child Health, leading the stem cell gene therapy programme. She oversees gene therapy trials for immune deficiencies, haematological, and metabolic disorders, focusing on developing novel treatments for immune disorders. Claire has extensive experience in leading first-in-human clinical trials and translating research into clinical practice. As an attending physician, she manages patients with immunodeficiencies, including stem cell transplants, with a particular interest in HLH disorders. Claire is an elected board member of the European and American Societies of Gene and Cell Therapy, holds an honorary position at Boston Children’s Hospital and Harvard Medical School, and co-founded the AGORA Foundation to improve access to gene therapies for ultra-rare diseases.

Presentation(s):

• PLENARY I: PRESIDENTIAL SYMPOSIUM

  Wednesday, June 11, 2025
  10:30 AM – 12:15 PM HK Time

• THE PRESENT AND FUTURE OF GENE THERAPIES FOR INBORN ERRORS OF IMMUNITY

  Thursday, June 12, 2025
  9:35 AM – 9:55 AM HK Time